Wang et al, J Child Neurol, 2007

Scala di valutazione CHOP INTEND

Scala HFMSE (Hammersmith Functional Motor Scale-Expanded)

Mercuri et al, 2017, Diagnosis and management of spinal muscular atrophy: Part 1

Finkel et al, 2017, Diagnosis and management of spinal muscular atrophy:
Part 2

Cerchi risorse per genitori/caregiver?

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